专题:Virus-based gene therapy research

This cluster of papers covers a wide range of topics related to gene therapy, including the use of viral vectors such as AAV and adenovirus, advancements in oncolytic virus therapy, hematopoietic stem cell gene therapy, immunodeficiency treatments, lentiviral vector applications, transgene expression, and genomic integration. The research reflects the ongoing progress and challenges in the field of gene therapy.
最新文献
Rewiring endogenous genes in CAR T cells for tumour-restricted payload delivery

article Full Text OpenAlex

AAV gene therapy for autosomal recessive deafness 9: a single-arm trial

article Full Text OpenAlex

CAR-T cells targeting CCR9 and CD1a for the treatment of T cell acute lymphoblastic leukemia

article Full Text OpenAlex

AAV mini-dystrophin gene therapy for Duchenne muscular dystrophy: a phase 1b trial

article Full Text OpenAlex

A Rare Case of Parvovirus Infection Causing Pure Red Cell Aplasia in a Kidney‐Pancreas Transplant Recipient

article Full Text OpenAlex

Combining Machine Learning and Multiplexed, In Situ Profiling to Engineer Cell Type and Behavioral Specificity

preprint Full Text OpenAlex

Measles oncolytic virus as an immunotherapy for recurrent/refractory pediatric medulloblastoma and atypical teratoid rhabdoid tumor: results from PNOC005

article Full Text OpenAlex

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B

article Full Text OpenAlex

Increasing Predominance of Norovirus GII.17 over GII.4, United States, 2022–2025

article Full Text OpenAlex

Intracerebroventricular bivalent CAR T cells targeting EGFR and IL-13Rα2 in recurrent glioblastoma: a phase 1 trial

article Full Text OpenAlex

近5年高被引文献
Safety and Efficacy of Single-Dose Ad26.COV2.S Vaccine against Covid-19

article Full Text OpenAlex 2432 FWCI326.287

CAR-T cell therapy: current limitations and potential strategies

review Full Text OpenAlex 2011 FWCI55.958

Interim Results of a Phase 1–2a Trial of Ad26.COV2.S Covid-19 Vaccine

article Full Text OpenAlex 1130 FWCI71.536

Viral vector platforms within the gene therapy landscape

review Full Text OpenAlex 1055 FWCI36.738

The current landscape of nucleic acid therapeutics

review Full Text OpenAlex 1044 FWCI25.267

Drug delivery systems for RNA therapeutics

review Full Text OpenAlex 931 FWCI32.296

Long-term outcomes following CAR T cell therapy: what we know so far

review Full Text OpenAlex 794 FWCI55.382

The furin cleavage site in the SARS-CoV-2 spike protein is required for transmission in ferrets

article Full Text OpenAlex 738 FWCI45.163

Overall Survival Benefit with Tebentafusp in Metastatic Uveal Melanoma

article Full Text OpenAlex 682 FWCI125.728

Virus-like particles: preparation, immunogenicity and their roles as nanovaccines and drug nanocarriers

review Full Text OpenAlex 672 FWCI24.038