专题：RNA regulation and disease

This cluster of papers explores the functions and regulation of RNA editing by ADAR deaminases, including its impact on gene regulation, innate immunity, microRNA processing, and the genomic landscape. It covers a wide range of topics such as neurological disorders, cancer, and transcriptome diversity.
最新文献
Limiting endosomal damage sensing reduces inflammation triggered by lipid nanoparticle endosomal escape

article Full Text OpenAlex

RNA lariat debranching enzyme (DBR1) variations in Sabinas brittle hair syndrome form of trichothiodystrophy (TTD): A TTD causing gene

article Full Text OpenAlex

MLKL Modulates Necroptosis and Neuroinflammation in a Mouse Model of MS

article Full Text OpenAlex

Cellular and biophysical barriers to lipid nanoparticle mediated delivery of RNA to the cytosol

article Full Text OpenAlex

AAV gene therapy for autosomal recessive deafness 9: a single-arm trial

article Full Text OpenAlex

Metachromatic Leukodystrophy

review Full Text OpenAlex

RIPK1 senses S-adenosylmethionine scarcity to drive cell death and inflammation

article Full Text OpenAlex

RNA codon expansion via programmable pseudouridine editing and decoding

article Full Text OpenAlex

Regulated localization of transposable element RNA during influenza A virus infection

article Full Text OpenAlex

The RNA-binding E3 ligase MKRN2 selectively disrupts Il6 translation to restrain inflammation

article Full Text OpenAlex

近5年高被引文献
CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis

article Full Text OpenAlex 1290 FWCI85.765

Strategies for delivering therapeutics across the blood–brain barrier

review Full Text OpenAlex 831 FWCI18.473

Inference of CRISPR Edits from Sanger Trace Data

article Full Text OpenAlex 641 FWCI48.387

Neurotoxic reactive astrocytes induce cell death via saturated lipids

article Full Text OpenAlex 474 FWCI41.236

Engineered virus-like particles for efficient in vivo delivery of therapeutic proteins

article Full Text OpenAlex 464 FWCI43.313

Lipids and Lipid Derivatives for RNA Delivery

review Full Text OpenAlex 460 FWCI10.305

In vivo base editing rescues Hutchinson–Gilford progeria syndrome in mice

article Full Text OpenAlex 405 FWCI28.095

Prime editing for precise and highly versatile genome manipulation

review Full Text OpenAlex 390 FWCI12.999

The Machinery of Exosomes: Biogenesis, Release, and Uptake

review Full Text OpenAlex 357 FWCI18.543

Senolysis by glutaminolysis inhibition ameliorates various age-associated disorders

article Full Text OpenAlex 346 FWCI42.247